Muscular Dystrophy UK is continuing to work closely with SMA UK, TreatSMA, clinicians and NHS England to ensure that people eligible for Spinraza are able to access it.
We want to hear from adults with SMA about Spinraza
Acaster Lloyd, an independent research consultancy, are carrying out research looking at the impact of Duchenne muscular dystrophy on family carers, including peoples experience with licenced treatments, like Translarna.