Muscular Dystrophy UK is continuing to work closely with SMA UK, TreatSMA, clinicians and NHS England to ensure that people eligible for Spinraza are able to access it.
We want to hear from adults with SMA about Spinraza
Acaster Lloyd, an independent research consultancy, are carrying out research looking at the impact of Duchenne muscular dystrophy on family carers, including peoples experience with licenced treatments, like Translarna.
Research in quality of life for Duchenne
Ways you can get involved
For over 50 years, we've been here for people living with muscle-wasting conditions. We couldn't do this without your help. Thank you.
Support for our work is more crucial than ever, so we've got lots of ideas about how you can help us fundraise.
Our brilliant volunteers help us deliver services, fundraise and raise awareness about muscle-wasting conditions.